Thursday, September 10, 2015

First Application of Sangamo's In Vivo Protein Replacement Platform (IVPRP) for Potential Cure of Hemophilia B

From today's press release:
"Hemophilia B is the first clinical application of our IVPRP which can be applied to many other diseases that are currently treated by protein replacement including hemophilia A and lysosomal storage disorders," said Geoff Nichol, M.B., Ch.B., Sangamo's executive vice president of research and development. "Successful review, by the NIH RAC, of the first human in vivo genome editing clinical protocol is a major milestone for Sangamo. We appreciate this careful consideration and unanimous approval of our proposed clinical trial and look forward to the commencement of our Phase 1 study in the near future."

IMPRESSIVE WORK !!

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